PTC Therapeutics Highlights Data on High Disease Burden and Value of Treatment Across Two Rare Diseases

PRNewswire

Nov 16, 2020

- AADC deficiency associated with high and accumulating disease burden, demonstrating the need for access to an effective therapy -

- Patient and caregiver quality of life study reveals real-life impact of nonsense mutation Duchenne muscular dystrophy and reinforces value of treatment -

PR Newswire

SOUTH PLAINFIELD, N.J., Nov. 16, 2020

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