BioMarin Receives Positive CHMP Opinion in Europe for Vosoritide for the Treatment of Children with Achondroplasia from Age 2 Until Growth Plates Close

PRNewswire

Jun 25, 2021

European Commission Decision expected Q3 2021

Temporary Authorization for Use (ATU) Granted in France to Allow Access and Reimbursement of Vosoritide to Begin Immediately

Vosoritide is Potentially the First Medicine to be Approved to Treat Children with Achondroplasia in Europe

Estimated Over 11,000 Children Across Europe, Middle East, and Africa Affected by Achondroplasia and Eligible for Treatment if Approved

FDA Review of Vosoritide NDA Ongoing, PDUFA Target Action Date Nov. 20, 2021

PR Newswire

SAN RAFAEL, Calif., June 25, 2021

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