PYC Therapeutics Announces Comprehensive Preclinical Results Demonstrating VP-002 Program's Potential as the First Disease Modifying Therapy for Autosomal Dominant Optic Atrophy

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Jun 29, 2021

PYC's Second Lead Program Being Developed for the Treatment of Autosomal Dominant Optic Atrophy (ADOA) Caused by Mutations in the OPA1 Gene, for Which There Are Currently No Approved Treatments or Drugs in Clinical Development

PYC's Differentiated PPMO Technology Results in Effective Delivery to Target Cells in the Retina in Vivo and Greater Than 1.5-Fold Upregulation of the Target OPA1 Protein and Correction of Major Functional Deficits in Patient-Derived Cells

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