Audentes Therapeutics Announces Next Steps in the Development of AT132 to Treat XLMTM Following Collaborative Initial Meeting with FDA Under RMAT Designation

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Jan 31, 2019
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Proceeding with previously announced plan to enroll 3 to 5 additional patients in Cohort 2 of the ASPIRO Phase 1/2 study and to select the optimal dose of AT132 in the second quarter of 2019

Subsequent to determination of the optimal dose, Audentes plans to provide an updated data package to FDA to facilitate final agreement on the path to BLA submission

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