Substantial Reduction in excess of 92% in Mean Bleed Rate Requiring Factor VIII Infusions; Sustained over the Period of Observation (3 Years in High Dose and 2 Years in Low Dose)
Rate of FVIII Change Continued to be Expression Level Dependent, Slowed in Year 3, and Appears to be Approaching Plateau
Conference Call and Webcast to be Held Tuesday, May 28, 2019 at 8:00 AM Eastern
PR Newswire
SAN RAFAEL, Calif., May 28, 2019